Topical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung disease (Q24245035)

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

A placebo-controlled study of liposome-mediated gene transfer to the nasal epithelium of patients with cystic fibrosis.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Airway epithelial CFTR mRNA expression in cystic fibrosis patients after repetitive administration of a recombinant adenovirus

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Repeat administration of DNA/liposomes to the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Aerosol and lobar administration of a recombinant adenovirus to individuals with cystic fibrosis. I. Methods, safety, and clinical implications

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

A controlled study of adenoviral-vector-mediated gene transfer in the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Evidence for safety and efficacy of DOTAP cationic liposome mediated CFTR gene transfer to the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Safety and biological efficacy of an adeno-associated virus vector-cystic fibrosis transmembrane regulator (AAV-CFTR) in the cystic fibrosis maxillary sinus.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Maxillary sinusitis as a surrogate model for CF gene therapy clinical trials in patients with antrostomies

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

A phase II, double-blind, randomized, placebo-controlled clinical trial of tgAAVCF using maxillary sinus delivery in patients with cystic fibrosis with antrostomies.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Repeat administration of an adenovirus vector encoding cystic fibrosis transmembrane conductance regulator to the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Comparison of DNA-lipid complexes and DNA alone for gene transfer to cystic fibrosis airway epithelia in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Cystic fibrosis: a worldwide analysis of CFTR mutations--correlation with incidence data and application to screening

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

New concepts of the pathogenesis of cystic fibrosis lung disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

The chest radiograph in cystic fibrosis: a new scoring system compared with the Chrispin-Norman and Brasfield scores

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Meta-analyses involving cross-over trials: methodological issues

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Barriers to and new approaches for gene therapy and gene delivery in cystic fibrosis.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Improved survival in the Danish center-treated cystic fibrosis patients: results of aggressive treatment.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Gene therapy for cystic fibrosis: an example for lung gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Pre-clinical and clinical endpoint assays for cystic fibrosis gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Measuring inconsistency in meta-analyses

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Systematic reviews in health care: Assessing the quality of controlled clinical trials

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Evidence for periciliary liquid layer depletion, not abnormal ion composition, in the pathogenesis of cystic fibrosis airways disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

The evolution of airway function in early childhood following clinical diagnosis of cystic fibrosis.

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Identification of the cystic fibrosis gene: cloning and characterization of complementary DNA

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

The phenotypic consequences of CFTR mutations

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Repeated Aerosolized AAV-CFTR for Treatment of Cystic Fibrosis: A Randomized Placebo-Controlled Phase 2B Trial

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

Safety and biological efficacy of a lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

7 January 2021

The changing epidemiology of cystic fibrosis

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

7 January 2021

Efficient and persistent gene transfer of AAV-CFTR in maxillary sinus

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

7 January 2021

A phase I study of adenovirus-mediated transfer of the human cystic fibrosis transmembrane conductance regulator gene to a lung segment of individuals with cystic fibrosis

1 reference

https://api.crossref.org/works/10.1002%2F14651858.CD005599.PUB2

7 January 2021