Imiglucerase in the management of Gaucher disease type 1: an evidence-based review of its place in therapy (Q28067032)

Sebastian Carballo

series ordinal

2

1 reference

Jacques Serratrice

series ordinal

3

1 reference

Jérome Stirnemann

series ordinal

4

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language of work or name

1 reference

14 October 2016

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1 reference

11

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page(s)

37-47

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Creative Commons Attribution-NonCommercial 3.0 Unported

copyright license

start time

1 October 2016

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

0 references

cites work

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Imiglucerase and its use for the treatment of Gaucher's disease

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Enzyme replacement therapy with taliglucerase alfa: 36-month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase

20 March 2017

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Biochemical response to substrate reduction therapy versus enzyme replacement therapy in Gaucher disease type 1 patients

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Clonal Immunoglobulin against Lysolipids in the Origin of Myeloma

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Long-term velaglucerase alfa treatment in children with Gaucher disease type 1 naïve to enzyme replacement therapy or previously treated with imiglucerase

29 September 2017

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Achievement of therapeutic goals with low-dose imiglucerase in Gaucher disease: a single-center experience

29 September 2017

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Glucosylsphingosine is a highly sensitive and specific biomarker for primary diagnostic and follow-up monitoring in Gaucher disease in a non-Jewish, Caucasian cohort of Gaucher disease patients

29 September 2017

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Effects of imiglucerase on the growth and metabolism of Gaucher disease type I patients: a systematic review

29 September 2017

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Did the temporary shortage in supply of imiglucerase have clinical consequences? Retrospective observational study on 34 italian Gaucher type I patients

29 September 2017

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Velaglucerase alfa enzyme replacement therapy compared with imiglucerase in patients with Gaucher disease

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Long-term clinical outcomes in type 1 Gaucher disease following 10 years of imiglucerase treatment

29 September 2017

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Mapping the genetic and clinical characteristics of Gaucher disease in the Iberian Peninsula.

29 September 2017

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Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease

29 September 2017

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Elevated plasma glucosylsphingosine in Gaucher disease: relation to phenotype, storage cell markers, and therapeutic response

29 September 2017

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Pulmonary vascular disease in Gaucher disease: clinical spectrum, determinants of phenotype and long-term outcomes of therapy

29 September 2017

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The management of pregnancy in Gaucher disease

29 September 2017

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Osteopenia in Gaucher disease develops early in life: response to imiglucerase enzyme therapy in children, adolescents and adults

29 September 2017

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Bone events and evolution of biologic markers in Gaucher disease before and during treatment

29 September 2017

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A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Phase 1/2 and extension study of velaglucerase alfa replacement therapy in adults with type 1 Gaucher disease: 48-month experience

29 September 2017

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Timing of initiation of enzyme replacement therapy after diagnosis of type 1 Gaucher disease: effect on incidence of avascular necrosis

29 September 2017

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The female Gaucher patient: the impact of enzyme replacement therapy around key reproductive events (menstruation, pregnancy and menopause).

29 September 2017

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'Non-neuronopathic' Gaucher disease reconsidered. Prevalence of neurological manifestations in a Dutch cohort of type I Gaucher disease patients and a systematic review of the literature.

29 September 2017

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Gaucher disease: mutation and polymorphism spectrum in the glucocerebrosidase gene (GBA).

29 September 2017

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Improvement of bone disease by imiglucerase (Cerezyme) therapy in patients with skeletal manifestations of type 1 Gaucher disease: results of a 48-month longitudinal cohort study

29 September 2017

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Clinical consequences of interrupting enzyme replacement therapy in children with type 1 Gaucher disease

29 September 2017

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Low frequency maintenance therapy with imiglucerase in adult type I Gaucher disease: a prospective randomized controlled trial.

29 September 2017

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Type 2 Gaucher disease: 15 new cases and review of the literature

29 September 2017

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Orthopedic considerations in Gaucher disease since the advent of enzyme replacement therapy

29 September 2017

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Therapeutic goals in the treatment of Gaucher disease.

29 September 2017

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French results of enzyme replacement therapy in Gaucher's disease

29 September 2017

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Molecular and cell biology of acid beta-glucosidase and prosaposin

29 September 2017

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The Gaucher registry: demographics and disease characteristics of 1698 patients with Gaucher disease

29 September 2017

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The role of neurogenetics in Gaucher disease

29 September 2017

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Marked elevation of plasma chitotriosidase activity. A novel hallmark of Gaucher disease

29 September 2017

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Leukocyte beta-glucosidase in homozygotes and heterozygotes for Gaucher disease

29 September 2017

1 reference

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Serum ferritin concentration in Gaucher's disease

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Demonstration of a deficiency of glucocerebroside-cleaving enzyme in Gaucher's disease

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Enzyme replacement therapy in Gaucher's disease: preliminary clinical trial of a new enzyme preparation

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Treatment of Gaucher's disease with liposome-entrapped glucocerebroside: beta-glucosidase

29 September 2017

1 reference

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29 September 2017

1 reference

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Replacement therapy for inherited enzyme deficiency. Use of purified glucocerebrosidase in Gaucher's disease.

2 June 2018

1 reference

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Glucosylsphingosine is a key biomarker of Gaucher disease

2 June 2018

1 reference

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Eliglustat compared with imiglucerase in patients with Gaucher's disease type 1 stabilised on enzyme replacement therapy: a phase 3, randomised, open-label, non-inferiority trial.

27 November 2018

1 reference

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Safety and efficacy results of switch from imiglucerase to velaglucerase alfa treatment in patients with type 1 Gaucher disease.

27 November 2018

1 reference

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B cell lymphoma and myeloma in murine Gaucher's disease.

27 November 2018

1 reference

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Successful pregnancy and lactation outcome in a patient with Gaucher disease receiving enzyme replacement therapy, and the subsequent distribution and excretion of imiglucerase in human breast milk.

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Eight-year clinical outcomes of long-term enzyme replacement therapy for 884 children with Gaucher disease type 1.

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

A benchmark analysis of the achievement of therapeutic goals for type 1 Gaucher disease patients treated with imiglucerase

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Imiglucerase (Cerezyme) improves quality of life in patients with skeletal manifestations of Gaucher disease.

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Correlation of surrogate markers of Gaucher disease. Implications for long-term follow up of enzyme replacement therapy

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

27 November 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

27 November 2018

Adult Gaucher disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Quality of life assessment in adults with type 1 Gaucher disease.

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Bone involvement in Gaucher disease

27 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5072572

Type I Gaucher disease in children with and without enzyme therapy

27 November 2018

1 reference

12 December 2020

Quality of life related to type 1 Gaucher disease: Spanish experience

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12 December 2020

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

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12 December 2020

Clinical evaluation of chemokine and enzymatic biomarkers of Gaucher disease

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12 December 2020

A randomized trial comparing the efficacy and safety of imiglucerase (Cerezyme) infusions every 4 weeks versus every 2 weeks in the maintenance therapy of adult patients with Gaucher disease type 1

1 reference

12 December 2020

Lung involvement and enzyme replacement therapy in Gaucher's disease

1 reference

12 December 2020

Delayed growth and puberty in patients with Gaucher disease type 1: natural history and effect of splenectomy and/or enzyme replacement therapy

1 reference

12 December 2020

Effect of enzyme replacement therapy with imiglucerase on BMD in type 1 Gaucher disease

1 reference

12 December 2020

Quantification of bone involvement in Gaucher disease: MR imaging bone marrow burden score as an alternative to Dixon quantitative chemical shift MR imaging--initial experience

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12 December 2020

Replacement therapy with imiglucerase for type 1 Gaucher's disease

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12 December 2020

Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources

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12 December 2020

Home treatment with intravenous enzyme replacement therapy for Gaucher disease: an international collaborative study of 33 patients

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12 December 2020

Use of enzyme replacement therapy for Gaucher disease during pregnancy

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12 December 2020

Enzyme replacement therapy for Gaucher disease

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12 December 2020

Serum chitotriosidase activity in Gaucher patients on enzyme replacement therapy (ERT)

1 reference

12 December 2020

Enzyme replacement therapy in type 1 and type 3 Gaucher's disease

1 reference

12 December 2020