Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer (Q28115950)

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Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer
scientific journal article

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    Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer (English)
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    J. H. Wolfe
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    M. S. Sands
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    J. E. Barker
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    B. Gwynn
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    L. B. Rowe
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    C. A. Vogler
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    E. H. Birkenmeier
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    24 December 2016
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    360
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    6406
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    749–753
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