Correction of SMN2 Pre-mRNA splicing by antisense U7 small nuclear RNAs (Q28277159)

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Sharlene R Lim

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Till Geib

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Bianca J Lam

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Klemens J Hertel

The genetic component in child mortality

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language of work or name

English

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publication date

December 2005

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published in

Molecular Therapy

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volume

12

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issue

6

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page(s)

1013-22

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cites work

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SMN oligomerization defect correlates with spinal muscular atrophy severity

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SMN, the product of the spinal muscular atrophy gene, binds preferentially to dimethylarginine-containing protein targets

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