Systemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher disease (Q28482370)

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Systemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher disease
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    Systemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher disease (English)
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    Mario A Cabrera-Salazar
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    Matthew Deriso
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    Scott D Bercury
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    Lingyun Li
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    John T Lydon
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    William Weber
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    Nilesh Pande
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    Mandy A Cromwell
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    Diane Copeland
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    John Leonard
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    Seng H Cheng
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    Ronald K Scheule
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    2012
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    7
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    e43310
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    8
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