Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series (Q34152598)
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English | Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series |
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Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series (English)
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Roberto Giugliani
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Christina Lampe
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Ann-Kathrin Bosserhoff
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Barbara K Burton
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Carolina F de Souza
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Camila Bittar
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Nicole Muschol
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Rebecca Olson
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Nancy J Mendelsohn
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