Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series (Q34152598)

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Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series
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    Long-term experience with enzyme replacement therapy (ERT) in MPS II patients with a severe phenotype: an international case series (English)
    Christina Lampe
    Ann-Kathrin Bosserhoff
    Barbara K Burton
    Carolina F de Souza
    Camila Bittar
    Nicole Muschol
    Rebecca Olson
    Nancy J Mendelsohn

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