Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies (Q34313390)

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Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies
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    Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies (English)
    Dominique P Germain
    Derralynn A Hughes
    Kathy Nicholls
    Laura Barisoni
    Charles J Jennette
    Alexander Bragat
    Jeff Castelli
    Sheela Sitaraman
    David J Lockhart
    Pol F Boudes
    24 November 2012

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