Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies (Q34313390)
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English | Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies |
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Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies (English)
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Roberto Giugliani
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Dominique P Germain
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Derralynn A Hughes
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Atul Mehta
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Kathy Nicholls
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Laura Barisoni
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Charles J Jennette
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Alexander Bragat
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Jeff Castelli
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Sheela Sitaraman
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David J Lockhart
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Pol F Boudes
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24 November 2012
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