Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B. (Q34343757)

1 August 2017

title

Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B. (English)

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1 August 2017

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Martin A Hausl

1

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1 August 2017

Wenli Zhang

2

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1 August 2017

Nadine Müther

3

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1 August 2017

Christina Rauschhuber

4

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1 August 2017

Helen G Franck

5

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1 August 2017

Elizabeth P Merricks

6

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1 August 2017

Timothy C Nichols

7

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1 August 2017

Mark A Kay

8

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1 August 2017

Anja Ehrhardt

9

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1 August 2017

language of work or name

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17 August 2010

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1 August 2017

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1 August 2017

volume

18

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1 August 2017

issue

11

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1 August 2017

page(s)

1896-1906

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Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates

1 August 2017

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Bioengineered factor IX molecules with increased catalytic activity improve the therapeutic index of gene therapy vectors for hemophilia B

6 July 2018

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6 July 2018

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6 July 2018

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6 July 2018

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6 July 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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Neonatal or hepatocyte growth factor-potentiated adult gene therapy with a retroviral vector results in therapeutic levels of canine factor IX for hemophilia B.

27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

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27 October 2018

Identifiers

DOI

10.1038/MT.2010.169

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1 August 2017

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1 August 2017

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