Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives (Q34354096)

1 August 2017

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title

Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives (English)

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1 August 2017

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Rolling F

1

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1 August 2017

language of work or name

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1 October 2004

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1 August 2017

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1 August 2017

11 Suppl 1

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1 August 2017

S26-32

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https://scigraph.springernature.com/pub.10.1038/sj.gt.3302366

1 August 2017

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cites work

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21 January 2018

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Rep/Cap gene amplification and high-yield production of AAV in an A549 cell line expressing Rep/Cap.

21 January 2018

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Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.

21 January 2018

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Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

21 January 2018

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Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector

21 January 2018

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Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

21 January 2018

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Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model

21 January 2018

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Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Gene transfer into the mouse retina mediated by an adeno-associated viral vector

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Adeno-associated virus gene transfer to mouse retina

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV.

21 January 2018

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Long-term protection of retinal structure but not function using RAAV.CNTF in animal models of retinitis pigmentosa

21 January 2018

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Reporter expression persists 1 year after adeno-associated virus-mediated gene transfer to the optic nerve

21 January 2018

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Sustained tetracycline-regulated transgene expression in vivo in rat retinal ganglion cells using a single type 2 adeno-associated viral vector

21 January 2018

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Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model

21 January 2018

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Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

21 January 2018

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Recombinant adeno-associated virus serotype 4 mediates unique and exclusive long-term transduction of retinal pigmented epithelium in rat, dog, and nonhuman primate after subretinal delivery

21 January 2018

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Virus-mediated transduction of murine retina with adeno-associated virus: effects of viral capsid and genome size.

21 January 2018

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Stable rAAV-mediated transduction of rod and cone photoreceptors in the canine retina

21 January 2018

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Adeno-associated virus type 5: transduction efficiency and cell-type specificity in the primate retina.

21 January 2018

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Immediate and long-term safety of recombinant adeno-associated virus injection into the nonhuman primate muscle

21 January 2018

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Functional and structural recovery of the retina after gene therapy in the RPE65 null mutation dog.

21 January 2018

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Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy.

21 January 2018

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AAV-Mediated gene transfer slows photoreceptor loss in the RCS rat model of retinitis pigmentosa

21 January 2018

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Two animal models of retinal degeneration are rescued by recombinant adeno-associated virus-mediated production of FGF-5 and FGF-18.

21 January 2018

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Glial cell line derived neurotrophic factor delays photoreceptor degeneration in a transgenic rat model of retinitis pigmentosa

21 January 2018

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A humanized system for pharmacologic control of gene expression

21 January 2018

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Regulated delivery of therapeutic proteins after in vivo somatic cell gene transfer.

21 January 2018

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Control of erythropoietin secretion by doxycycline or mifepristone in mice bearing polymer-encapsulated engineered cells

21 January 2018

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Ecdysone-inducible gene expression in mammalian cells and transgenic mice.

21 January 2018

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Tight control of gene expression in mammalian cells by tetracycline-responsive promoters

21 January 2018

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Transcriptional activation by tetracyclines in mammalian cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Pharmacological regulation of protein expression from adeno-associated viral vectors in the eye.

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Long-term control of erythropoietin secretion by doxycycline in mice transplanted with engineered primary myoblasts

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Lack of an immune response against the tetracycline-dependent transactivator correlates with long-term doxycycline-regulated transgene expression in nonhuman primates after intramuscular injection of recombinant adeno-associated virus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Recombinant AAV-mediated delivery of a tet-inducible reporter gene to the rat retina

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Hypoxia-regulated transgene expression in experimental retinal and choroidal neovascularization

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Molecular ophthalmology: an update on animal models for retinal degenerations and dystrophies

21 January 2018

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PEDF: Raising both hopes and questions in controlling angiogenesis

21 January 2018

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21 January 2018

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Prevention of experimental choroidal neovascularization with intravitreal anti-vascular endothelial growth factor antibody fragment.

21 January 2018

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Angiostatin: A novel angiogenesis inhibitor that mediates the suppression of metastases by a lewis lung carcinoma

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Endostatin: an endogenous inhibitor of angiogenesis and tumor growth

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Prevention of ischemia-induced retinopathy by the natural ocular antiangiogenic agent pigment epithelium-derived factor

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Adeno-associated virus type-2 expression of pigmented epithelium-derived factor or Kringles 1-3 of angiostatin reduce retinal neovascularization

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Inhibition of retinal neovascularisation by gene transfer of soluble VEGF receptor sFlt-1.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Potential long-term inhibition of ocular neovascularisation by recombinant adeno-associated virus-mediated secretion gene therapy

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Apoptosis: final common pathway of photoreceptor death in rd, rds, and rhodopsin mutant mice

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Retinal neuroprotection by growth factors: a mechanistic perspective

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

AAV-mediated delivery of ciliary neurotrophic factor prolongs photoreceptor survival in the rhodopsin knockout mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Effects of adeno-associated virus-vectored ciliary neurotrophic factor on retinal structure and function in mice with a P216L rds/peripherin mutation

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2Rd2/Rd2 model of retinal degeneration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Long-term evaluation of retinal function in Prph2Rd2/Rd2 mice following AAV-mediated gene replacement therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Improvement of neuronal visual responses in the superior colliculus in Prph2(Rd2/Rd2) mice following gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Mutations in MERTK, the human orthologue of the RCS rat retinal dystrophy gene, cause retinitis pigmentosa

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Correction of the retinal dystrophy phenotype of the RCS rat by viral gene transfer of Mertk

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Vitamin A metabolism in the retinal pigment epithelium: genes, mutations, and diseases

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

In utero gene therapy rescues vision in a murine model of congenital blindness

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Pigment epithelium-derived factor: a potent inhibitor of angiogenesis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

7 January 2021

inferred from DOI database lookup

Intravitreal gene therapy reduces lysosomal storage in specific areas of the CNS in mucopolysaccharidosis VII mice.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

7 January 2021

inferred from DOI database lookup

Inhibition of retinal neovascularization by intraocular viral-mediated delivery of anti-angiogenic agents

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302366

7 January 2021

inferred from DOI database lookup

Identifiers

DOI

10.1038/SJ.GT.3302366

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Dimensions Publication ID

1 August 2017

1042835605

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Fatcat ID

release_ck24ok5xlfgeddnk3hfyv437lm

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/ck24ok5xlfgeddnk3hfyv437lm

24 November 2022

mapped directly with Wikidata item

1 reference