Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study (Q34389992)
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English | Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study |
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Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo-controlled study (English)
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Vassili Valayannopoulos
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Eugen Mengel
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Roberto Giugliani
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Christian J Hendriksz
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Barbara Burton
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Thomas R Fleming
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Paul Harmatz
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Derralynn Hughes
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Simon A Jones
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Shuan-Pei Lin
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Maurizio Scarpa
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STRIVE Investigators
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Peter Slasor
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Debra Lounsbury
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Wolfgang Dummer
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