A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency (Q34493345)

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A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency
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    A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency (English)
    Barbara K Burton
    Manisha Balwani
    François Feillet
    T Andrew Burrow
    Carmen Camarena Grande
    Mahmut Coker
    Alejandra Consuelo-Sánchez
    Patrick Deegan
    Maja Di Rocco
    Gregory M Enns
    Richard Erbe
    Fatih Ezgu
    Katryn N Furuya
    Christina Laukaitis
    Edward G Neilan
    Scott Nightingale
    Heidi Peters
    Maurizio Scarpa
    K Otfried Schwab
    Vratislav Smolka
    Marnie Wood
    Zachary Goodman
    Yijun Yang
    Stephen Eckert
    Sandra Rojas-Caro
    Anthony G Quinn
    1 September 2015
    1010-1020

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