Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants (Q34501456)
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English | Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants |
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Pharmacological chaperone corrects lysosomal storage in Fabry disease caused by trafficking-incompetent variants (English)
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Gary Hin-Fai Yam
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Nils Bosshard
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Christian Zuber
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Beat Steinmann
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Jürgen Roth
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