Multiplex CRISPR/Cas9-based genome engineering from a single lentiviral vector (Q34509983)

2 August 2017

Multiplex CRISPR/Cas9-based genome engineering from a single lentiviral vector (English)

1 reference

2 August 2017

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Ami M Kabadi

1

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2 August 2017

David G Ousterout

series ordinal

2

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2 August 2017

Isaac B Hilton

series ordinal

3

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2 August 2017

Charles A Gersbach

series ordinal

4

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2 August 2017

language of work or name

English

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publication date

13 August 2014

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2 August 2017

Nucleic Acids Research

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2 August 2017

42

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2 August 2017

e147

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2 August 2017

19

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Creative Commons Attribution 4.0 International

2 August 2017

start time

3 May 2017

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April 2022 Public Data File from Crossref

copyright status

copyrighted

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cites work

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Phylogeny of Cas9 determines functional exchangeability of dual-RNA and Cas9 among orthologous type II CRISPR-Cas systems

7 July 2018

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Orthogonal Cas9 proteins for RNA-guided gene regulation and editing

7 July 2018

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Locus-specific editing of histone modifications at endogenous enhancers

7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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Reading frame correction by targeted genome editing restores dystrophin expression in cells from Duchenne muscular dystrophy patients.

7 July 2018

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ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

7 July 2018

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7 July 2018

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7 July 2018

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7 July 2018

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RNA-programmed genome editing in human cells

7 July 2018

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Targeted genome engineering in human cells with the Cas9 RNA-guided endonuclease

7 July 2018

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Efficient genome editing in zebrafish using a CRISPR-Cas system

7 July 2018

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7 July 2018

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Multiplex genome engineering using CRISPR/Cas systems

7 July 2018

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Targeted methylation and gene silencing of VEGF-A in human cells by using a designed Dnmt3a-Dnmt3L single-chain fusion protein with increased DNA methylation activity

7 July 2018

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Light-inducible spatiotemporal control of gene activation by customizable zinc finger transcription factors

7 July 2018

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Advances in targeted genome editing

7 July 2018

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A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity

7 July 2018

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Gene targeting to the ROSA26 locus directed by engineered zinc finger nucleases

7 July 2018

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In situ genetic correction of the sickle cell anemia mutation in human induced pluripotent stem cells using engineered zinc finger nucleases

7 July 2018

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Site-specific gene correction of a point mutation in human iPS cells derived from an adult patient with sickle cell disease

7 July 2018

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In vivo genome editing restores haemostasis in a mouse model of haemophilia

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4231726

A rapid and general assay for monitoring endogenous gene modification

7 July 2018

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Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome

7 July 2018

1 reference

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Lentiviral vector gene therapy: effective and safe?

7 July 2018

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Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases

7 July 2018

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Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4231726

Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

7 July 2018

1 reference

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A novel approach for the construction of multiple shRNA expression vectors

7 July 2018

1 reference

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Highly efficient endogenous human gene correction using designed zinc-finger nucleases

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4231726

An unusually compact external promoter for RNA polymerase III transcription of the human H1RNA gene

7 July 2018

1 reference

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Regulation of an endogenous locus using a panel of designed zinc finger proteins targeted to accessible chromatin regions. Activation of vascular endothelial growth factor A.

7 July 2018

1 reference

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Chemically regulated zinc finger transcription factors

7 July 2018

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Synthetic zinc finger transcription factor action at an endogenous chromosomal site. Activation of the human erythropoietin gene

7 July 2018

1 reference

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Nucleotide sequences of mouse genomic loci including a gene or pseudogene for U6 (4.8S) nuclear RNA.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4231726

The in vitro transcription of the 7SK RNA gene by RNA polymerase III is dependent only on the presence of an upstream promoter.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4231726

Synergistic and tunable human gene activation by combinations of synthetic transcription factors

7 July 2018

1 reference

Crossref

https://api.crossref.org/works/10.1093%2FNAR%2FGKU749

Self-processing of ribozyme-flanked RNAs into guide RNAs in vitro and in vivo for CRISPR-mediated genome editing

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1093%2FNAR%2FGKU749

21 January 2018

Identifiers

DOI

10.1093/NAR/GKU749

1 reference

2 August 2017

1 reference

2 August 2017

1 reference