MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression (Q34621747)

3 August 2017

MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression (English)

1 reference

3 August 2017

1 reference

Jui-Hung Hung

5

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Stefan L Ameres

object named as

Stefan L Ameres

4

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Phillip D. Zamore

object named as

Phillip D Zamore

17

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Craig Mello

14

object named as

Craig C Mello

1 reference

3 August 2017

Jun Xie

1

1 reference

3 August 2017

Qing Xie

2

1 reference

3 August 2017

Hongwei Zhang

3

1 reference

3 August 2017

Qin Su

6

1 reference

3 August 2017

Ran He

7

1 reference

3 August 2017

Xin Mu

8

1 reference

3 August 2017

Seemin Seher Ahmed

9

1 reference

3 August 2017

Soyeon Park

10

1 reference

3 August 2017

Hiroki Kato

11

1 reference

3 August 2017

Chengjian Li

12

1 reference

3 August 2017

Christian Mueller

13

1 reference

3 August 2017

Zhiping Weng

15

1 reference

3 August 2017

Terence R Flotte

16

1 reference

3 August 2017

Guangping Gao

18

1 reference

3 August 2017

21 December 2010

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3 August 2017

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3 August 2017

19

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3 August 2017

526-535

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3 August 2017

3

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A phase I study of aromatic L-amino acid decarboxylase gene therapy for Parkinson's disease

3 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Target RNA-directed trimming and tailing of small silencing RNAs

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB).

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Invited review: festschrift edition of neurosurgery peripheral nervous system as a conduit for delivering therapies for diabetic neuropathy, amyotrophic lateral sclerosis, and nerve regeneration

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

AAV as a gene transfer vector for the treatment of neurological disorders: novel treatment thoughts for ALS.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Molecular signatures of disease brain endothelia provide new sites for CNS-directed enzyme therapy

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Safety evaluation of AAV2-GDNF gene transfer into the dopaminergic nigrostriatal pathway in aged and parkinsonian rhesus monkeys

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Exploiting and antagonizing microRNA regulation for therapeutic and experimental applications

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Effect of tissue-specific promoters and microRNA recognition elements on stability of transgene expression after hydrodynamic naked plasmid DNA delivery

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

MicroRNAs: target recognition and regulatory functions

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Tailoring the AAV vector capsid for gene therapy.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Harnessing endogenous miRNAs to control virus tissue tropism as a strategy for developing attenuated virus vaccines

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

A let-7 MicroRNA-sensitive vesicular stomatitis virus demonstrates tumor-specific replication

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Safety and tolerability of gene therapy with an adeno-associated virus (AAV) borne GAD gene for Parkinson's disease: an open label, phase I trial

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

miR-122, a mammalian liver-specific microRNA, is processed from hcr mRNA and may downregulate the high affinity cationic amino acid transporter CAT-1.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Expression profiling identifies microRNA signature in pancreatic cancer

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

miRBase: the microRNA sequence database

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Silencing of microRNAs in vivo with 'antagomirs'

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Adeno-associated viruses undergo substantial evolution in primates during natural infections

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Identification of tissue-specific microRNAs from mouse

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

A proteinase inhibitor II of Solanum americanum is expressed in phloem.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

RNA interference is mediated by 21- and 22-nucleotide RNAs

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Clinicopathological findings following intraventricular glial-derived neurotrophic factor treatment in a patient with Parkinson's disease

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Neonatal intraperitoneal or intravenous injections of recombinant adeno-associated virus type 8 transduce dorsal root ganglia and lower motor neurons

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

MicroRNA directs mRNA cleavage of the transcription factor NAC1 to downregulate auxin signals for arabidopsis lateral root development.

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3048189

miR-122a-regulated expression of a suicide gene prevents hepatotoxicity without altering antitumor effects in suicide gene therapy

26 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21179009

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

A controlled trial of riluzole in amyotrophic lateral sclerosis. ALS/Riluzole Study Group

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21179009

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Gene therapy for Parkinson's disease

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21179009

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

miR-122a-Regulated Expression of a Suicide Gene Prevents Hepatotoxicity Without Altering Antitumor Effects in Suicide Gene Therapy

1 reference

11 October 2022

https://opencitations.net/index/coci/api/v1/references/10.1038/MT.2010.279

Identifiers

DOI

10.1038/MT.2010.279

1 reference

3 August 2017

1 reference

3 August 2017

1 reference