Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines (Q35079584)

6 August 2017

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title

Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines (English)

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6 August 2017

2

C G Steward

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National Marrow Donor Program

6 August 2017

series ordinal

3

object named as

National Marrow Donor Program

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6 August 2017

C Peters

1

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6 August 2017

International Bone Marrow Transplant Registry

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4

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6 August 2017

Working Party on Inborn Errors, European Bone Marrow Transplant Group

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5

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6 August 2017

language of work or name

English

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publication date

1 February 2003

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Bone Marrow Transplantation

6 August 2017

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6 August 2017

31

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6 August 2017

229-239

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6 August 2017

4

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https://scigraph.springernature.com/pub.10.1038/sj.bmt.1703839

6 August 2017

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Clinical and biochemical outcome of marrow transplantation for Gaucher disease of the Norrbottnian type

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21 January 2018

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21 January 2018

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21 January 2018

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HLA-haploidentical blood progenitor cell transplantation in osteopetrosis

21 January 2018

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Wolman disease successfully treated by bone marrow transplantation.

21 January 2018

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The p38 mitogen-activated protein kinase pathway plays a critical role in thrombin-induced endothelial chemokine production and leukocyte recruitment

21 January 2018

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Allogeneic mesenchymal stem cell infusion for treatment of metachromatic leukodystrophy (MLD) and Hurler syndrome (MPS-IH).

21 January 2018

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Hematopoietic stem-cell transplantation in globoid-cell leukodystrophy

21 January 2018

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7 January 2021

Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-linked adrenoleukodystrophy

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7 January 2021

Bone-Marrow Transplantation in the Maroteaux–Lamy Syndrome (Mucopolysaccharidosis Type VI)

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7 January 2021

Treatment of MPS VII (Sly disease) by allogeneic BMT in a female with homozygous A619V mutation

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7 January 2021

Ocular changes in the mucopolysaccharidoses after bone marrow transplantation. A preliminary report

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7 January 2021

Evaluation of coronary artery disease in the Hurler syndrome by angiography

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https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Resting Tl-201 scintigraphy in the evaluation of coronary artery disease in children with Hurler syndrome.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Coronary artery patency following long-term successful engraftment 14 years after bone marrow transplantation in the Hurler syndrome

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https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Follow-up of nine patients with Hurler syndrome after bone marrow transplantation.

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https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation

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https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Long-term effects of bone marrow transplantation for inborn errors of metabolism: a study of four patients with lysosomal storage diseases.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow transplantation for Sanfilippo disease type B

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

MR spectroscopic imaging of normal-appearing white matter in adrenoleukodystrophy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Reversal of early neurologic and neuroradiologic manifestations of X-linked adrenoleukodystrophy by bone marrow transplantation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Treatment of Late Infantile Metachromatic Leukodystrophy by Bone Marrow Transplantation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow-derived mesenchymal stem cells remain host-derived despite successful hematopoietic engraftment after allogeneic transplantation in patients with lysosomal and peroxisomal storage diseases

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Long-term follow-up of the first successful bone marrow transplantation in Gaucher disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone-marrow transplantation in severe Gaucher's disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Regression of the radiological changes of Gaucher's disease following bone marrow transplantation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow transplantation for the treatment of alpha-mannosidosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow transplantation for aspartylglucosaminuria: follow-up study of transplanted and non-transplanted patients

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Neuronal ceroid lipofuscinoses in childhood

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Hematopoietic cell transplantation in fetal lambs with ceroid-lipofuscinosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Batten's disease: failure of allogeneic bone marrow transplantation to arrest disease progression in a canine model.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Biochemical improvement after treatment by bone marrow transplantation in I-cell disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Improvement of tear lysosomal enzyme levels after treatment with bone marrow transplantation in a patient with I-cell disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow transplantation in canine GM1 gangliosidosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Cells that resorb bone

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone marrow transplantation for autosomal recessive osteopetrosis. A report from the Working Party on Inborn Errors of the European Bone Marrow Transplantation Group

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Hematopoietic stem cell transplantation for infantile osteopetrosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Allogeneic bone-marrow transplantation in infantile malignant osteopetrosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Bone-marrow transplantation for immunodeficiencies and osteopetrosis: European survey, 1968-1985

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Imaging of malignant infantile osteopetrosis before and after bone marrow transplantation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.BMT.1703839

7 January 2021

Identifiers

DOI

10.1038/SJ.BMT.1703839

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Dimensions Publication ID

6 August 2017

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1 reference