Hereditary inclusion body myopathy: single patient response to intravenous dosing of GNE gene lipoplex (Q35575697)
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scientific article published on 25 April 2011
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English | Hereditary inclusion body myopathy: single patient response to intravenous dosing of GNE gene lipoplex |
scientific article published on 25 April 2011 |
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Hereditary inclusion body myopathy: single patient response to intravenous dosing of GNE gene lipoplex (English)
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John Nemunaitis
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Gregory Nemunaitis
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Chris M Jay
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Phillip B Maples
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William A Gahl
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Marjan Huizing
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Tal Yardeni
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Alex W Tong
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Anagha P Phadke
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Beena O Pappen
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Cynthia Bedell
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Henry Allen
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Cathy Hernandez
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Nancy S Templeton
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Joseph Kuhn
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Neil Senzer
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25 April 2011
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