Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis I (Q35600310)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

title

Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis I (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

main subject

gene therapy

0 references

mucopolysaccharidosis I

1 reference

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

James Wilson

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

author name string

Christian Hinderer

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Peter Bell

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Qiang Wang

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Jean-Pierre Louboutin

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Yanqing Zhu

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Jessica Bagel

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Patricia O'Donnell

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Tracey Sikora

9

1 reference

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9 March 2020

Therese Ruane

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Ping Wang

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

Mark E Haskins

12

1 reference

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9 March 2020

publication date

16 July 2014

1 reference

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9 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

volume

22

1 reference

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9 March 2020

issue

12

1 reference

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9 March 2020

page(s)

2018-2027

1 reference

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describes a project that uses

9 March 2020

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC4429692/fullTextXML

inferred from PubMed Central ID database lookup

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Specific antibody titer alters the effectiveness of intrathecal enzyme replacement therapy in canine mucopolysaccharidosis I.

12 July 2018

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Glycosaminoglycan storage in neuroanatomical regions of mucopolysaccharidosis I dogs following intrathecal recombinant human iduronidase

12 July 2018

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Biodistribution and pharmacodynamics of recombinant human alpha-L-iduronidase (rhIDU) in mucopolysaccharidosis type I-affected cats following multiple intrathecal administrations

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Direct gene transfer to the CNS prevents emergence of neurologic disease in a murine model of mucopolysaccharidosis type I.

12 July 2018

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Heparin cofactor II-thrombin complex and dermatan sulphate:chondroitin sulphate ratio are biomarkers of short- and long-term treatment effects in mucopolysaccharide diseases

12 July 2018

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12 July 2018

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7 January 2021

Cervical pachymeningeal hypertrophy as the initial and cardinal manifestation of mucopolysaccharidosis type I in monozygotic twins with a novel mutation in the alpha-L-iduronidase gene

1 reference

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7 January 2021

Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I

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7 January 2021

Intrathecal enzyme replacement therapy in a patient with mucopolysaccharidosis type I and symptomatic spinal cord compression

1 reference

https://api.crossref.org/works/10.1038%2FMT.2014.135

7 January 2021

Identifiers

DOI

10.1038/MT.2014.135

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25027660%20AND%20SRC:MED&resulttype=core&format=json

9 March 2020

1 reference