Compassionate use of orphan drugs (Q35986747)

11 August 2017

Compassionate use of orphan drugs (English)

1 reference

11 August 2017

1 reference

1 reference

Hanna I Hyry

1

1 reference

11 August 2017

Jeremy Manuel

series ordinal

2

1 reference

11 August 2017

Timothy M Cox

series ordinal

3

1 reference

11 August 2017

Jonathan C P Roos

series ordinal

4

1 reference

11 August 2017

21 August 2015

1 reference

Orphanet Journal of Rare Diseases

11 August 2017

1 reference

11 August 2017

10

1 reference

11 August 2017

100

1 reference

Orphan drugs: expensive yet necessary.

11 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

The European Gaucher Alliance: a survey of member patient organisations' activities, healthcare environments and concerns

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

World Medical Association Declaration of Helsinki: ethical principles for medical research involving human subjects

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

The legal imperative for treating rare disorders

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

Temporary authorization for use: does the French patient access programme for unlicensed medicines impact market access after formal licensing?

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

Compassionate use of interventions: results of a European Clinical Research Infrastructures Network (ECRIN) survey of ten European countries

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

Force majeure: therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

Limits on use of health economic assessments for rare diseases

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4546220

Confusion reigns over compassionate use of AIDS drug

24 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26292942

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Orphan drug pricing may warrant a competition law investigation

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26292942

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1186/S13023-015-0306-X

1 reference

Dimensions Publication ID

11 August 2017

0 references

1 reference

11 August 2017

PubMed publication ID

26292942

1 reference