Clinical outcomes following hematopoietic stem cell transplantation for the treatment of mucopolysaccharidosis VI (Q36009130)

11 August 2017

Clinical outcomes following hematopoietic stem cell transplantation for the treatment of mucopolysaccharidosis VI (English)

1 reference

11 August 2017

mucopolysaccharidosis VI

1 reference

Sean Turbeville

1

1 reference

11 August 2017

Helen Nicely

2

1 reference

11 August 2017

J Douglas Rizzo

3

1 reference

11 August 2017

Tanya L Pedersen

4

1 reference

11 August 2017

Paul J Orchard

5

1 reference

11 August 2017

Mitchell E Horwitz

6

1 reference

11 August 2017

Edwin M Horwitz

7

1 reference

11 August 2017

Paul Veys

8

1 reference

11 August 2017

Carmem Bonfim

9

1 reference

11 August 2017

Amal Al-Seraihy

10

1 reference

11 August 2017

25 October 2010

1 reference

Molecular Genetics and Metabolism

11 August 2017

1 reference

11 August 2017

102

1 reference

11 August 2017

2

1 reference

11 August 2017

111-115

1 reference

Transplant outcomes in mucopolysaccharidoses

11 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Lysosomal storage disorders in the newborn

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Mucopolysaccharidosis VI: the Italian experience

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Mucopolysaccharidoses in the Scandinavian countries: incidence and prevalence

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Hematopoietic cell therapy for metabolic disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Management guidelines for mucopolysaccharidosis VI.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

New therapeutic options for lysosomal storage disorders: enzyme replacement, small molecules and gene therapy

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Trends in haematopoietic cell transplantation for inborn errors of metabolism

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

National Institutes of Health consensus development project on criteria for clinical trials in chronic graft-versus-host disease: I. Diagnosis and staging working group report

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Allogeneic stem cell transplantation for the treatment of lysosomal and peroxisomal metabolic diseases

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Cord-blood transplants from unrelated donors in patients with Hurler's syndrome

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

The status of hematopoietic stem cell transplantation in lysosomal storage disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Lysosomal storage disorders: emerging therapeutic options require early diagnosis

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Insights into the diagnosis and treatment of lysosomal storage diseases

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

1994 Consensus Conference on Acute GVHD Grading

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Bone marrow transplantation for Maroteaux-Lamy syndrome (MPS VI): long-term follow-up.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Risk factor analysis of outcomes after unrelated cord blood transplantation in patients with hurler syndrome

11 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Update and actual trends on bacterial infections following liver transplantation

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Combination of enzyme replacement and hematopoietic stem cell transplantation as therapy for Hurler syndrome.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3367500

Chromosomal localization of ARSB, the gene for human N-acetylgalactosamine-4-sulphatase

23 September 2018

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Cumulative incidence rates of the mucopolysaccharidoses in Germany

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Threshold effect of urinary glycosaminoglycans and the walk test as indicators of disease progression in a survey of subjects with Mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Mucopolysaccharidosis VI.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Outcomes of hematopoietic stem cell transplantation for Hurler's syndrome in Europe: a risk factor analysis for graft failure

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

The MPS I registry: design, methodology, and early findings of a global disease registry for monitoring patients with Mucopolysaccharidosis Type I

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Improved metabolic correction in patients with lysosomal storage disease treated with hematopoietic stem cell transplant compared with enzyme replacement therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Bone-Marrow Transplantation in the Maroteaux–Lamy Syndrome (Mucopolysaccharidosis Type VI)

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

Long-term follow-up of a girl with Maroteaux-Lamy syndrome after bone marrow transplantation

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2010.09.010

10.1016/J.YMGME.2010.09.010

7 January 2021

Identifiers

DOI

1 reference

release_7wowgcxopbfm3isecjnn7vka6q

11 August 2017

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/7wowgcxopbfm3isecjnn7vka6q

mapped directly with Wikidata item

24 November 2022

based on heuristic

1 reference

11 August 2017

1 reference