CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy (Q36030998)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25741864%20AND%20SRC:MED&resulttype=core&format=json

2 March 2020

title

CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy (English)

1 reference

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2 March 2020

1

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2 March 2020

Zoheb Kazi

2

1 reference

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2 March 2020

Catherine W Rehder

7

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2 March 2020

Anna Tylki-Szymańska

11

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2 March 2020

14

Priya S Kishnani

1 reference

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2 March 2020

author name string

Sean N Prater

3

1 reference

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2 March 2020

Deeksha S Bali

4

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2 March 2020

Jennifer Goldstein

5

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2 March 2020

Mihaela C Stefanescu

6

1 reference

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2 March 2020

Eleanor G Botha

8

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2 March 2020

Carolyn Ellaway

9

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2 March 2020

Kaustuv Bhattacharya

10

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2 March 2020

Nesrin Karabul

12

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2 March 2020

Amy S Rosenberg

13

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2 March 2020

language of work or name

English

0 references

publication date

5 March 2015

1 reference

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2 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25741864%20AND%20SRC:MED&resulttype=core&format=json

2 March 2020

volume

17

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2 March 2020

issue

11

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2 March 2020

page(s)

912-918

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https://scigraph.springernature.com/pub.10.1038/gim.2015.6

2 March 2020

exact match

0 references

cites work

Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Algorithm for the early diagnosis and treatment of patients with cross reactive immunologic material-negative classic infantile pompe disease: a step towards improving the efficacy of ERT.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Bortezomib in the rapid reduction of high sustained antibody titers in disorders treated with therapeutic protein: lessons learned from Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Persistence of high sustained antibodies to enzyme replacement therapy despite extensive immunomodulatory therapy in an infant with Pompe disease: need for agents to target antibody-secreting plasma cells

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Predicting cross-reactive immunological material (CRIM) status in Pompe disease using GAA mutations: lessons learned from 10 years of clinical laboratory testing experience

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Atypical immunologic response in a patient with CRIM-negative Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: lessons learned from infantile Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Chinese hamster ovary cell-derived recombinant human acid alpha-glucosidase in infantile-onset Pompe disease

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Left ventricular myocardial mass determined by cross-sectional echocardiography in normal newborns, infants, and children

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

CRIM-Negative Pompe Disease Patients with Satisfactory Clinical Outcomes on Enzyme Replacement Therapy

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Letter to the Editors: Concerning "CRIM-negative Pompe disease patients with satisfactory clinical outcomes on enzyme replacement therapy" by Al Khallaf et al.

11 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

CRIM-negative infantile Pompe disease: 42-month treatment outcome.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Elimination of antibodies to recombinant enzyme in Pompe's disease.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4561024

Nonparametric Estimation from Incomplete Observations

23 September 2018

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FGIM.2015.6

Nephrotic syndrome complicating alpha-glucosidase replacement therapy for Pompe disease

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25741864

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/GIM.2015.6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25741864%20AND%20SRC:MED&resulttype=core&format=json

release_rtpv52li4fdplnrfxf3zgxjjri

2 March 2020

Fatcat ID

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/rtpv52li4fdplnrfxf3zgxjjri

mapped directly with Wikidata item

24 November 2022

based on heuristic

Microsoft Academic ID

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25741864%20AND%20SRC:MED&resulttype=core&format=json

2 March 2020

1 reference