In silico and in vitro evaluation of exonic and intronic off-target effects form a critical element of therapeutic ASO gapmer optimization. (Q36160667)

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23 February 2020

title

In silico and in vitro evaluation of exonic and intronic off-target effects form a critical element of therapeutic ASO gapmer optimization (English)

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23 February 2020

4

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23 February 2020

author name string

Piotr J Kamola

1

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23 February 2020

Jeremy D A Kitson

2

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23 February 2020

Gemma Turner

3

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23 February 2020

Sofie Eriksson

5

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23 February 2020

Aliza Panjwani

6

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23 February 2020

Linda C Warnock

7

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23 February 2020

Gaelle A Douillard Guilloux

8

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23 February 2020

Kitty Moores

9

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23 February 2020

Emma L Koppe

10

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23 February 2020

William E Wixted

11

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23 February 2020

Paul A Wilson

12

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23 February 2020

Nigel J Gooderham

13

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23 February 2020

Timothy W Gant

14

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23 February 2020

Kenneth L Clark

15

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23 February 2020

Stephen A Hughes

16

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23 February 2020

Mark R Edbrooke

17

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23 February 2020

Joel D Parry

18

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23 February 2020

language of work or name

English

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publication date

3 September 2015

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23 February 2020

published in

Nucleic Acids Research

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23 February 2020

volume

43

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23 February 2020

issue

18

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23 February 2020

page(s)

8638-8650

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Creative Commons Attribution-NonCommercial 4.0 International

23 February 2020

copyright license

start time

7 November 2016

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

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PubMed

https://pubmed.ncbi.nlm.nih.gov/26338776

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12 December 2020

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Identifiers

DOI

10.1093/NAR/GKV857

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23 February 2020

1 reference

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23 February 2020

1 reference

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