What Is the Purpose of the Orphan Drug Act? (Q36237799)

12 August 2017

What Is the Purpose of the Orphan Drug Act? (English)

1 reference

12 August 2017

1 reference

Matthew Herder

1

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PMCID

5207521

12 August 2017

language of work or name

English

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publication date

3 January 2017

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12 August 2017

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12 August 2017

14

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12 August 2017

1

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12 August 2017

e1002191

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Creative Commons Attribution 4.0 International

12 August 2017

start time

3 January 2017

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

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cites work

Biomarker-Defined Subsets of Common Diseases: Policy and Economic Implications of Orphan Drug Act Coverage

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Orphan drug incentives in the pharmacogenomic context: policy responses in the US and Canada

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Funding innovation for treatment for rare diseases: adopting a cost-based yardstick approach.

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Paying for the Orphan Drug System: break or bend? Is it time for a new evaluation system for payers in Europe to take account of new rare disease treatments?

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Orphan drug development: an economically viable strategy for biopharma R&D.

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

An empirical review of major legislation affecting drug development: past experiences, effects, and unintended consequences.

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Pricing and reimbursement of orphan drugs: the need for more transparency

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Pregnant women deserve better

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

The US Orphan Drug Act: rare disease research stimulator or commercial opportunity?

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Drugs for neglected diseases: a failure of the market and a public health failure?

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Potential interactions of the Orphan Drug Act and pharmacogenomics: a flood of orphan drugs and abuses?

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5207521

Pharmacogenetic interventions, orphan drugs, and distributive justice: the role of cost-benefit analysis

22 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/28045908

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1371/JOURNAL.PMED.1002191

1 reference

12 August 2017

1 reference

12 August 2017

1 reference

PMCID

5207521