Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression (Q36754605)
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scientific article published on October 2009
Language | Label | Description | Also known as |
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English | Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression |
scientific article published on October 2009 |
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Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression (English)
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Baodong Sun
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Haoyue Zhang
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Andrew Bird
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Songtao Li
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Sarah P Young
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Dwight D Koeberl
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