Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression (Q36754605)

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scientific article published on October 2009
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English
Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression
scientific article published on October 2009

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    Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression (English)
    Baodong Sun
    Haoyue Zhang
    Andrew Bird
    Songtao Li
    Sarah P Young
    Dwight D Koeberl
    1 October 2009
    913-920

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