A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells (Q36782735)

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scientific article published on 10 February 2016
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A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
scientific article published on 10 February 2016

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    A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells (English)
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    Courtney S Young
    Michael R Hicks
    Natalia V Ermolova
    Saravanan Karumbayaram
    Chino Kumagai-Cresse
    Atsushi Nakano
    M Carrie Miceli
    Melissa J Spencer

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