Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy (Q36953239)
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scientific article published on 20 June 2013
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English | Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy |
scientific article published on 20 June 2013 |
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Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy (English)
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Sean N Prater
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Trusha T Patel
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Anne F Buckley
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Hanna Mandel
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Eugene Vlodavski
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Suhrad G Banugaria
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Erin J Feeney
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Nina Raben
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Priya S Kishnani
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20 June 2013
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