Miglustat: substrate reduction therapy for lysosomal storage disorders associated with primary central nervous system involvement (Q37067355)
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scientific article published on January 2006
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English | Miglustat: substrate reduction therapy for lysosomal storage disorders associated with primary central nervous system involvement |
scientific article published on January 2006 |
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Miglustat: substrate reduction therapy for lysosomal storage disorders associated with primary central nervous system involvement (English)
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Gregory M Pastores
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1 January 2006
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77-82
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