Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges (Q38042670)
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scientific article published on January 2012
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English | Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges |
scientific article published on January 2012 |
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Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges (English)
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R J Desnick
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E H Schuchman
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1 January 2012
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13
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307-335
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