A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome (Q38293234)

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A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome
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    A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome (English)
    Leanne K Winner
    Helen Beard
    Sofia Hassiotis
    Amanda J Luck
    15 March 2016
    363-375

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