Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice (Q39042768)
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scientific article published on 6 February 2015
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English | Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice |
scientific article published on 6 February 2015 |
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Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice (English)
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Maria Dahl
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Alexander Doyle
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Karin Olsson
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Jan-Eric Månsson
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André R A Marques
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Mina Mirzaian
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Johannes M Aerts
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Mats Ehinger
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Michael Rothe
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Ute Modlich
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Stefan Karlsson
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6 February 2015
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