Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial. (Q39691004)

From Wikidata

Jump to navigation Jump to search

scientific article published on 8 June 2016

Language	Label	Description	Also known as
English	Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.	scientific article published on 8 June 2016

Statements

scholarly article

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial (English)

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

phase I clinical trial

0 references

0 references

phase II clinical trial

0 references

metachromatic leukodystrophy

1 reference

based on heuristic

inferred from title

Francesca Fumagalli

3

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Andrea Calabria

10

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Paola M V Rancoita

13

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Angelo Quattrini

22

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Eugenio Montini

23

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Alessandro Aiuti

27

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

28

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

25

object named as

Fabio Ciceri

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Maria Grazia Roncarolo

26

object named as

Maria Grazia Roncarolo

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Francesco Morena

object named as

Francesco Morena

9

0 references

object named as

Maria Sessa

1

0 references

Clelia Di Serio

24

object named as

Clelia Di Serio

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

author name string

Laura Lorioli

2

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Serena Acquati

4

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Daniela Redaelli

5

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Cristina Baldoli

6

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Sabrina Canale

7

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Ignazio D Lopez

8

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Rossana Fiori

11

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Paolo Silvani

12

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Michela Gabaldo

14

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Fabrizio Benedicenti

15

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Gigliola Antonioli

16

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Andrea Assanelli

17

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Maria Pia Cicalese

18

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Ubaldo Del Carro

19

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Maria Grazia Natali Sora

20

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Sabata Martino

21

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Alessandra Biffi

29

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

language of work or name

0 references

publication date

8 June 2016

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

number of pages

12

1 reference

based on heuristic

inferred from page(s)

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

388

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

476-487

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

10043

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Metachromatic leukodystrophy--an update

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Juvenile metachromatic leukodystrophy 10 years post transplant compared with a non-transplanted cohort

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Neurodevelopmental outcomes of umbilical cord blood transplantation in metachromatic leukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Improvement of White Matter Changes on Neuroimaging Modalities After Stem Cell Transplant in Metachromatic Leukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Transplant outcomes in leukodystrophies

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Hematopoietic stem cell transplantation in the leukodystrophies: a systematic review of the literature

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort report.

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Outcome of Early Juvenile Onset Metachromatic Leukodystrophy After Unrelated Cord Blood Transplantation: A Case Series and Review of the Literature.

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Metachromatic leukodystrophy - mutation analysis provides further evidence of genotype-phenotype correlation

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Foot pad skin biopsy in mouse models of hereditary neuropathy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Development and reliability of a system to classify gross motor function in children with cerebral palsy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

The natural course of gross motor deterioration in metachromatic leukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Metachromatic leukodystrophy: natural course of cerebral MRI changes in relation to clinical course.

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Electrophysiologic correlates of peripheral nervous system maturation in infancy and childhood

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Peripheral motor and sensory nerve conduction studies in normal infants and children

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Amelioration of nerve conduction velocity following simultaneous kidney/pancreas transplantation is due to the glycaemic control provided by the pancreas.

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Lentiviral vector common integration sites in preclinical models and a clinical trial reflect a benign integration bias and not oncogenic selection

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

HIV-1 integration in the human genome favors active genes and local hotspots

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Language and cognition in children with metachromatic leukodystrophy: onset and natural course in a nationwide cohort

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model.

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Brain conditioning is instrumental for successful microglia reconstitution following hematopoietic stem cell transplantation

1 reference

https://api.crossref.org/works/10.1016%2FS0140-6736%2816%2930374-9

7 January 2021

based on heuristic

inferred from DOI database lookup

Identifiers

10.1016/S0140-6736(16)30374-9

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

1 reference

Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27289174%20AND%20SRC:MED&resulttype=core&format=json

13 March 2020

Sitelinks

Wikipedia(0 entries)

Wikibooks(0 entries)

Wikinews(0 entries)

Wikiquote(0 entries)

Wikisource(0 entries)

Wikiversity(0 entries)

Wikivoyage(0 entries)

Wiktionary(0 entries)

Multilingual sites(0 entries)

Retrieved from "https://www.wikidata.org/w/index.php?title=Q39691004&oldid=1939048114"