Functional repair of a mutant chloride channel using a trans-splicing ribozyme (Q39740174)

14 September 2017

Functional repair of a mutant chloride channel using a trans-splicing ribozyme (English)

1 reference

14 September 2017

0 references

Christopher S Rogers

1

1 reference

14 September 2017

Carlos G Vanoye

series ordinal

2

1 reference

14 September 2017

Bruce A Sullenger

series ordinal

3

1 reference

14 September 2017

Alfred L George

series ordinal

4

1 reference

14 September 2017

language of work or name

English

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publication date

1 December 2002

1 reference

Journal of Clinical Investigation

14 September 2017

1 reference

14 September 2017

110

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14 September 2017

12

1 reference

14 September 2017

1783-1789

1 reference

Emerging clinical applications of RNA

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Significantly higher activity of a cytoplasmic hammerhead ribozyme than a corresponding nuclear counterpart: engineered tRNAs with an extended 3' end can be exported efficiently and specifically to the cytoplasm in mammalian cells

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

RNA repair: a novel approach to gene therapy

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Enhancing RNA repair efficiency by combining trans-splicing ribozymes that recognize different accessible sites on a target RNA.

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Induction of wild-type p53 activity in human cancer cells by ribozymes that repair mutant p53 transcripts

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

mRNA localization signals can enhance the intracellular effectiveness of hammerhead ribozymes

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Tethering ribozymes to a retroviral packaging signal for destruction of viral RNA.

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Ribozyme-mediated repair of defective mRNA by targeted, trans-splicing

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

RNA chaperones and the RNA folding problem

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Improved patch-clamp techniques for high-resolution current recording from cells and cell-free membrane patches

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

One binding site determines sequence specificity of Tetrahymena pre-rRNA self-splicing, trans-splicing, and RNA enzyme activity

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

New reactions of the ribosomal RNA precursor of Tetrahymena and the mechanism of self-splicing

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Myotonia. An evaluation of the chloride hypothesis

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Controlled, targeted, intracellular expression of ribozymes: progress and problems

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Oligonucleotide scanning of native mRNAs in extracts predicts intracellular ribozyme efficiency: ribozyme-mediated reduction of the murine DNA methyltransferase

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

A missense mutation in canine C1C-1 causes recessive myotonia congenita in the dog.

25 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Ribozyme-mediated trans-splicing of a trinucleotide repeat.

25 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Mechanism of voltage-dependent gating in skeletal muscle chloride channels

25 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Tagging ribozyme reaction sites to follow trans-splicing in mammalian cells

25 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Cell cycle dependence of gene transfer by lipoplex, polyplex and recombinant adenovirus

15 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Spliceosome-mediated RNA trans-splicing as a tool for gene therapy

20 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

RNA localization: different zipcodes, same postman?

20 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Ribozyme-mediated repair of sickle beta-globin mRNAs in erythrocyte precursors

20 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Trans -splicing ribozymes for targeted gene delivery 1 1Edited by J. Karn

20 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=151654

Transcriptional control of the cell cycle

2 December 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/12488428

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Evaluating and enhancing ribozyme reaction efficiency in mammalian cells

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/12488428

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Aging-associated down-regulation of ClC-1 expression in skeletal muscle: phenotypic-independent relation to the decrease of chloride conductance

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/12488428

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1172/JCI200216481

1 reference

14 September 2017

1 reference

14 September 2017

1 reference