Antisense oligonucleotide treatment for a pseudoexon-generating mutation in the NPC1 gene causing Niemann-Pick type C disease (Q43283385)

From Wikidata
Jump to navigation Jump to search
scientific article published in November 2009
edit
Language Label Description Also known as
English
Antisense oligonucleotide treatment for a pseudoexon-generating mutation in the NPC1 gene causing Niemann-Pick type C disease
scientific article published in November 2009

    Statements

    Antisense oligonucleotide treatment for a pseudoexon-generating mutation in the NPC1 gene causing Niemann-Pick type C disease (English)
    Laura Rodríguez-Pascau
    Maria Josep Coll
    Lluïsa Vilageliu
    1 November 2009
    E993-E1001

    Identifiers

     
    edit
      edit
        edit
          edit
            edit
              edit
                edit
                  edit
                    edit