Miglustat in patients with Niemann-Pick disease Type C (NP-C): a multicenter observational retrospective cohort study (Q43298156)
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scientific article published on 4 August 2009
Language | Label | Description | Also known as |
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English | Miglustat in patients with Niemann-Pick disease Type C (NP-C): a multicenter observational retrospective cohort study |
scientific article published on 4 August 2009 |
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Miglustat in patients with Niemann-Pick disease Type C (NP-C): a multicenter observational retrospective cohort study (English)
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M Pineda
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J E Wraith
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E Mengel
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F Sedel
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B Bembi
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G C Korenke
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T Marquardt
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C Luzy
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R Giorgino
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4 August 2009
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