Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors (Q44052705)

29 November 2017

Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors (English)

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29 November 2017

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glycogen storage disease

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Beaty RM

1

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29 November 2017

Jackson M

2

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29 November 2017

Peterson D

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29 November 2017

Bird A

4

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29 November 2017

Brown T

5

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29 November 2017

Benjamin DK Jr

6

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29 November 2017

Juopperi T

7

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29 November 2017

Kishnani P

8

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29 November 2017

Boney A

9

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29 November 2017

Chen YT

10

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29 November 2017

Koeberl DD

11

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1 August 2002

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9

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15

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1015-1022

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https://scigraph.springernature.com/pub.10.1038/sj.gt.3301728

29 November 2017

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cites work

Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Sustained correction of bleeding disorder in hemophilia B mice by gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Recombinant adeno-associated virus for muscle directed gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Glycogen storage disease in adults

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Type I glycogen storage disease: nine years of management with cornstarch

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Biochemical evidence for the requirement of continuous glucose therapy in young adults with type 1 glycogen storage disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Glycogen storage disease type Ia in two littermate Maltese puppies.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Isolation and nucleotide sequence of canine glucose-6-phosphatase mRNA: identification of mutation in puppies with glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Canine model and genomic structural organization of glycogen storage disease type Ia (GSD Ia).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Liver transplantation for glycogen storage disease types I, III, and IV

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Correction of glycogen storage disease type 1a in a mouse model by gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Successful treatment of severe Type I glycogen storage disease with neonatal presentation by nocturnal intragastric feeding

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Nonrandom transduction of recombinant adeno-associated virus vectors in mouse hepatocytes in vivo: cell cycling does not influence hepatocyte transduction

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Persistent, therapeutically relevant levels of human granulocyte colony-stimulating factor in mice after systemic delivery of adeno-associated virus vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

An albumin enhancer located 10 kb upstream functions along with its promoter to direct efficient, liver-specific expression in transgenic mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Introns increase transcriptional efficiency in transgenic mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Improved adeno-associated virus vector production with transfection of a single helper adenovirus gene, E4orf6.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

Pulmonary hypertension in glycogen storage disease type I

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Progressive pulmonary hypertension: a fatal complication of type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Effect of continuous glucose therapy begun in infancy on the long-term clinical course of patients with type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Glomerular and tubular function in glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Metabolic control and renal dysfunction in type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

The kinetics of rAAV integration in the liver

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Production and characterization of improved adenovirus vectors with the E1, E2b, and E3 genes deleted

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3301728

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3301728

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release_r3oryxvo4nfi5hyqc3asgenogy

29 November 2017

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Fatcat

https://api.fatcat.wiki/v0/release/r3oryxvo4nfi5hyqc3asgenogy

24 November 2022

mapped directly with Wikidata item

1 reference