Attenuation of ganglioside GM1 accumulation in the brain of GM1 gangliosidosis mice by neonatal intravenous gene transfer (Q44538377)

3 December 2017

title

Attenuation of ganglioside GM1 accumulation in the brain of GM1 gangliosidosis mice by neonatal intravenous gene transfer (English)

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3 December 2017

Takaura N

1

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3 December 2017

Yagi T

2

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3 December 2017

Maeda M

3

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3 December 2017

Nanba E

4

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3 December 2017

Oshima A

5

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3 December 2017

Suzuki Y

6

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3 December 2017

Yamano T

7

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3 December 2017

Tanaka A

8

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3 December 2017

publication date

1 August 2003

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3 December 2017

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3 December 2017

volume

10

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3 December 2017

issue

17

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3 December 2017

page(s)

1487-1493

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Adenovirus-mediated gene transfer and expression of human beta-glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice

3 December 2017

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Long-term expression and transfer of arylsulfatase A into brain of arylsulfatase A-deficient mice transplanted with bone marrow expressing the arylsulfatase A cDNA from a retroviral vector

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Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.

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Intraventricular administration of recombinant adenovirus to neonatal twitcher mouse leads to clinicopathological improvements

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Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function

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Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy

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A mechanism of paraquat toxicity involving nitric oxide synthase

21 January 2018

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Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer

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Beta-galactosidase-deficient mouse as an animal model for GM1-gangliosidosis

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Molecular cloning of mouse acid beta-galactosidase cDNA: sequence, expression of catalytic activity and comparison with the human enzyme

21 January 2018

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A rapid and sensitive method for the quantitation of microgram quantities of protein utilizing the principle of protein-dye binding

21 January 2018

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Targeted disruption of the mouse sphingolipid activator protein gene: a complex phenotype, including severe leukodystrophy and wide-spread storage of multiple sphingolipids.

21 January 2018

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7 January 2021

Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation

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7 January 2021

Long-term effects of bone marrow transplantation for inborn errors of metabolism: a study of four patients with lysosomal storage diseases

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7 January 2021

Interendothelial junctional changes underlie the developmental 'tightening' of the blood-brain barrier.

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7 January 2021

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7 January 2021

Generalized CNS disease and massive GM1-ganglioside accumulation in mice defective in lysosomal acid beta-galactosidase

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7 January 2021

Quantitative estimation of sialic acids. II. A colorimetric resorcinol-hydrochloric acid method

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7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302033

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3 December 2017

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