Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells (Q44960581)

7 December 2017

title

Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells (English)

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7 December 2017

A Aartsma-Rus

1

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7 December 2017

W E Kaman

2

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7 December 2017

M Bremmer-Bout

3

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7 December 2017

A A M Janson

4

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7 December 2017

J T den Dunnen

5

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7 December 2017

G-J B van Ommen

6

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7 December 2017

J C T van Deutekom

7

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7 December 2017

publication date

1 September 2004

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7 December 2017

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7 December 2017

volume

11

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7 December 2017

issue

18

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7 December 2017

page(s)

1391-1398

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Novel antisense and peptide nucleic acid strategies for controlling gene expression

7 December 2017

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Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

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Additive antisense effects of different PNAs on the in vitro translation of the PML/RARalpha gene

21 January 2018

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21 January 2018

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21 January 2018

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7 January 2021

Dystrophin-associated protein abnormalities in dystrophin-deficient muscle fibers from symptomatic and asymptomatic Duchenne/Becker muscular dystrophy carriers

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7 January 2021

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7 January 2021

Deletion of individual exons and induction of soluble murine interleukin-5 receptor-alpha chain expression through antisense oligonucleotide-mediated redirection of pre-mRNA splicing.

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7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302313

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7 December 2017

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