Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C. (Q44985264)
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English | Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C. |
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Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C. (English)
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Danielle te Vruchte
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Emyr Lloyd-Evans
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Gabriele Reinkensmeier
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Daniel J Sillence
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Luisa Fernandez-Guillen
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Raymond A Dwek
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Terry D Butters
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Timothy M Cox
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1 August 2004
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16
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3
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654-658
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