Transgenic mouse expressing human mutant alpha-galactosidase A in an endogenous enzyme deficient background: a biochemical animal model for studying active-site specific chaperone therapy for Fabry disease (Q45129138)

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scientific article published in November 2004
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Transgenic mouse expressing human mutant alpha-galactosidase A in an endogenous enzyme deficient background: a biochemical animal model for studying active-site specific chaperone therapy for Fabry disease
scientific article published in November 2004

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    Transgenic mouse expressing human mutant alpha-galactosidase A in an endogenous enzyme deficient background: a biochemical animal model for studying active-site specific chaperone therapy for Fabry disease (English)
    Satoshi Ishii
    Hidekatsu Yoshioka
    Kazuaki Mannen
    Ashok B Kulkarni
    Jian-Qiang Fan
    1 November 2004
    250-257

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