Functional correction of CNS phenotypes in a lysosomal storage disease model using adeno-associated virus type 4 vectors. (Q45423330)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

title

Functional correction of CNS phenotypes in a lysosomal storage disease model using adeno-associated virus type 4 vectors (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

lysosomal storage disease

8 January 2020

main subject

vector-borne disease

0 references

1 reference

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

author name string

Gumei Liu

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

Inês Martins

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

John A Chiorini

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

Beverly L Davidson

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

language of work or name

English

0 references

publication date

1 October 2005

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

published in

Journal of Neuroscience

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

volume

25

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

issue

41

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

page(s)

9321-9327

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

Systemic hyperosmolality improves beta-glucuronidase distribution and pathology in murine MPS VII brain following intraventricular gene transfer

8 January 2020

cites work

1 reference

12 December 2020

Mammalian neural stem cells

1 reference

12 December 2020

Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system.

1 reference

12 December 2020

Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.

1 reference

12 December 2020

Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.

1 reference

12 December 2020

In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.

1 reference

12 December 2020

The HIV Tat protein transduction domain improves the biodistribution of beta-glucuronidase expressed from recombinant viral vectors.

1 reference

12 December 2020

Neurobiology of Pavlovian fear conditioning.

1 reference

12 December 2020

Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

1 reference

12 December 2020

Distribution of a lysosomal enzyme in the adult brain by axonal transport and by cells of the rostral migratory stream.

1 reference

12 December 2020

Selective neurodegeneration in murine mucopolysaccharidosis VII is progressive and reversible.

1 reference

12 December 2020

The place of the hippocampus in fear conditioning

1 reference

12 December 2020

Brain transplantation of genetically engineered human neural stem cells globally corrects brain lesions in the mucopolysaccharidosis type VII mouse

1 reference

12 December 2020

Evidence for bulk flow of brain interstitial fluid: significance for physiology and pathology

1 reference

12 December 2020

Adeno-associated virus 2-mediated gene therapy decreases autofluorescent storage material and increases brain mass in a murine model of infantile neuronal ceroid lipofuscinosis

1 reference

12 December 2020

Adeno-associated virus type 4 (AAV4) targets ependyma and astrocytes in the subventricular zone and RMS.

1 reference

12 December 2020

Defining the pathway for Tat-mediated delivery of beta-glucuronidase in cultured cells and MPS VII mice.

1 reference

12 December 2020

Immunological and neuropathological significance of the Virchow-Robin space

1 reference

12 December 2020

A murine model of mucopolysaccharidosis VII. Gross and microscopic findings in beta-glucuronidase-deficient mice

1 reference

12 December 2020

Interrelationships of the pia mater and the perivascular (Virchow-Robin) spaces in the human cerebrum

1 reference

12 December 2020

Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency

1 reference

12 December 2020

The biogenesis of lysosomes

1 reference

12 December 2020

Lysosomal enzymes and their receptors

1 reference

12 December 2020

Evidence for a 'paravascular' fluid circulation in the mammalian central nervous system, provided by the rapid distribution of tracer protein throughout the brain from the subarachnoid space

1 reference

12 December 2020

A method for microscopic studies of cerebral angioarchitecture and vascular-parenchymal relationships, based on the demonstration of 'paravascular' fluid pathways in the mammalian central nervous system.

1 reference

12 December 2020

Hurler and Hunter syndromes: mutual correction of the defect in cultured fibroblasts

1 reference

12 December 2020

Inborn errors of mucopolysaccharide metabolism

1 reference

12 December 2020

Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis

1 reference

12 December 2020

The ependyma: a protective barrier between brain and cerebrospinal fluid.

1 reference

12 December 2020

Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII.

1 reference

12 December 2020

Enzyme replacement therapy for murine mucopolysaccharidosis type VII

1 reference

12 December 2020

Behavioural abnormalities in a murine model of a human lysosomal storage disease.

1 reference

12 December 2020

Neuropathology of murine mucopolysaccharidosis type VII.

1 reference

12 December 2020

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase

1 reference

12 December 2020

Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles.

1 reference

12 December 2020

Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function

1 reference

12 December 2020

Prevalence of lysosomal storage disorders

1 reference

12 December 2020

10.1523/JNEUROSCI.2936-05.2005

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16221840%20AND%20SRC:MED&resulttype=core&format=json

8 January 2020

1 reference