Efficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector (Q45428790)

14 December 2017

Efficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector (English)

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14 December 2017

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Martha Campbell-Thompson

8

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14 December 2017

Thomas J Conlon

1

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14 December 2017

Travis Cossette

2

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14 December 2017

Kirsten Erger

3

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14 December 2017

Young-Kook Choi

4

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14 December 2017

Tracy Clarke

5

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14 December 2017

Marda Scott-Jorgensen

6

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14 December 2017

Sihong Song

7

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14 December 2017

James Crawford

9

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14 December 2017

Terence R Flotte

10

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14 December 2017

8 August 2005

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14 December 2017

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14 December 2017

12

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5

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14 December 2017

867-875

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Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha 1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults

14 December 2017

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Use of a highly purified alpha 1-antitrypsin standard to establish ranges for the common normal and deficient alpha 1-antitrypsin phenotypes

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Evaluation of the S-type of alpha-1-antitrypsin as an in vivo and in vitro inhibitor of neutrophil elastase

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Replacement therapy for alpha 1-antitrypsin deficiency associated with emphysema

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Augmentation of lung antineutrophil elastase capacity with recombinant human alpha-1-antitrypsin

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Adenovirus-mediated transfer of a recombinant alpha 1-antitrypsin gene to the lung epithelium in vivo

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Ex vivo and in vivo gene transfer to the skin using replication-deficient recombinant adenovirus vectors

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell line

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I vector expressing AAV-2 Rep and Cap.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Detection of infectious adeno-associated virus particles in human cervical biopsies

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

DNA-dependent PK inhibits adeno-associated virus DNA integration

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Intramuscular administration of recombinant adeno-associated virus 2 alpha-1 antitrypsin (rAAV-SERPINA1) vectors in a nonhuman primate model: safety and immunologic aspects

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Efficient ex vivo transduction of pancreatic islet cells with recombinant adeno-associated virus vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Characterization of the transcription profile of adeno-associated virus type 5 reveals a number of unique features compared to previously characterized adeno-associated viruses

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Effect of DNA-dependent protein kinase on the molecular fate of the rAAV2 genome in skeletal muscle

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Rapid uncoating of vector genomes is the key to efficient liver transduction with pseudotyped adeno-associated virus vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

Recent developments and current status of gene therapy using viral vectors in the United Kingdom

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.05.016

10.1016/J.YMTHE.2005.05.016

7 January 2021

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14 December 2017

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