CNS-directed AAV2-mediated gene therapy ameliorates functional deficits in a murine model of infantile neuronal ceroid lipofuscinosis. (Q45889316)

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10 January 2020

title

CNS-directed AAV2-mediated gene therapy ameliorates functional deficits in a murine model of infantile neuronal ceroid lipofuscinosis (English)

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Infantile neuronal ceroid lipofuscinosis

10 January 2020

main subject

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8

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10 January 2020

Annie E Wentz

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10 January 2020

Mark S Sands

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10 January 2020

author name string

Megan A Griffey

1

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10 January 2020

David Wozniak

2

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10 January 2020

Michael Wong

3

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10 January 2020

Ellen Bible

4

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10 January 2020

Kendra Johnson

5

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10 January 2020

Steven M Rothman

6

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publication date

20 December 2005

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10 January 2020

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10 January 2020

volume

13

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10 January 2020

issue

3

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10 January 2020

page(s)

538-547

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The neuronal ceroid-lipofuscinoses (Batten disease): a new class of lysosomal storage diseases

10 January 2020

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