Long-term monitoring of patients with infantile-onset Pompe disease on enzyme replacement therapy using a urinary glucose tetrasaccharide biomarker. (Q45972040)
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English | Long-term monitoring of patients with infantile-onset Pompe disease on enzyme replacement therapy using a urinary glucose tetrasaccharide biomarker. |
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Long-term monitoring of patients with infantile-onset Pompe disease on enzyme replacement therapy using a urinary glucose tetrasaccharide biomarker. (English)
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Beth L Thurberg
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Deeksha Bali
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Priya S Kishnani
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Sarah P Young
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Haoyue Zhang
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Deyanira Corzo
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David S Millington
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1 July 2009
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11
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536-541
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