Efficacy of systemic morpholino exon-skipping in Duchenne dystrophy dogs (Q46087408)

26 June 2018

title

Efficacy of systemic morpholino exon-skipping in Duchenne dystrophy dogs (English)

1 reference

26 June 2018

author name string

Toshifumi Yokota

1

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26 June 2018

Qi-Long Lu

2

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26 June 2018

Terence Partridge

3

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26 June 2018

Masanori Kobayashi

4

1 reference

26 June 2018

Akinori Nakamura

5

1 reference

26 June 2018

Shińichi Takeda

6

1 reference

26 June 2018

Eric Hoffman

7

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26 June 2018

publication date

1 June 2009

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26 June 2018

published in

Annals of Neurology

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26 June 2018

volume

65

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26 June 2018

issue

6

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26 June 2018

page(s)

667-676

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26 June 2018

describes a project that uses

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC5951302/fullTextXML

inferred from PubMed Central ID database lookup

cites work

A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new ground

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Optimizing exon skipping therapies for DMD.

30 June 2018

1 reference

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Sustained dystrophin expression induced by peptide-conjugated morpholino oligomers in the muscles of mdx mice.

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Follow-up of three patients with a large in-frame deletion of exons 45-55 in the Duchenne muscular dystrophy (DMD) gene

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy.

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Cardiac involvement in Beagle-based canine X-linked muscular dystrophy in Japan (CXMDJ): electrocardiographic, echocardiographic, and morphologic studies

30 June 2018

1 reference

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Induction of revertant fibres in the mdx mouse using antisense oligonucleotides

30 June 2018

1 reference

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Functional analysis of 114 exon-internal AONs for targeted DMD exon skipping: indication for steric hindrance of SR protein binding sites

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

30 June 2018

1 reference

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Flow cytometric characterization of myogenic cell populations obtained via the preplate technique: potential for rapid isolation of muscle-derived stem cells

30 June 2018

1 reference

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Loss of the sarcoglycan complex and sarcospan leads to muscular dystrophy in beta-sarcoglycan-deficient mice

30 June 2018

1 reference

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Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides

30 June 2018

1 reference

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Morpholino antisense oligomers: design, preparation, and properties

30 June 2018

1 reference

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Dystrophin-glycoprotein complex: its role in the molecular pathogenesis of muscular dystrophies.

30 June 2018

1 reference

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Dystrophin: the protein product of the Duchenne muscular dystrophy locus

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD.

30 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

15 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype

15 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Restoration of dystrophin expression in mdx mice by intravascular injection of naked DNA containing full-length dystrophin cDNA.

15 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Ultrasound-mediated transfection of canine myocardium by intravenous administration of cationic microbubble-linked plasmid DNA.

15 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

An explanation for the constitutive exon 9 cassette splicing of the DMD gene

15 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5951302

Exploring the frontiers of therapeutic exon skipping for Duchenne muscular dystrophy by double targeting within one or multiple exons

15 August 2018

1 reference

12 December 2020

Canine X-linked muscular dystrophy in Japan (CXMDJ)

1 reference

12 December 2020

Local dystrophin restoration with antisense oligonucleotide PRO051

1 reference

12 December 2020

An error in dystrophin mRNA processing in golden retriever muscular dystrophy, an animal homologue of Duchenne muscular dystrophy

1 reference

12 December 2020

Major clinical and histopathological characteristics of canine X-linked muscular dystrophy in Japan, CXMDJ

1 reference

12 December 2020

Expansion of revertant fibers in dystrophic mdx muscles reflects activity of muscle precursor cells and serves as an index of muscle regeneration

1 reference

12 December 2020

Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy

1 reference

12 December 2020

Identifiers

DOI

10.1002/ANA.21627

1 reference

26 June 2018

PMC publication ID

5951302

1 reference

26 June 2018

PubMed publication ID

19288467

1 reference

26 June 2018