Biochemical, pathological, and skeletal improvement of mucopolysaccharidosis VI after gene transfer to liver but not to muscle. (Q46936588)

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9 January 2020

title

Biochemical, pathological, and skeletal improvement of mucopolysaccharidosis VI after gene transfer to liver but not to muscle (English)

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9 January 2020

main subject

mucopolysaccharidosis VI

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9

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9 January 2020

author name string

Alessandra Tessitore

1

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9 January 2020

Armida Faella

2

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9 January 2020

Thomas O'Malley

3

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9 January 2020

Gabriella Cotugno

4

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9 January 2020

Monica Doria

5

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9 January 2020

Tetsuo Kunieda

6

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9 January 2020

Giuseppe Matarese

7

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9 January 2020

Mark Haskins

8

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9 January 2020

publication date

23 October 2007

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9 January 2020

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9 January 2020

volume

16

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9 January 2020

issue

1

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9 January 2020

page(s)

30-37

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The status of hematopoietic stem cell transplantation in lysosomal storage disease

9 January 2020

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