Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase). (Q48463259)
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scientific article published on 4 June 2007
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English | Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase). |
scientific article published on 4 June 2007 |
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Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase). (English)
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J Edmond Wraith
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Michael Beck
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Roderick Lane
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Ans van der Ploeg
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Elsa Shapiro
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Yong Xue
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Emil D Kakkis
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Nathalie Guffon
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4 June 2007
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120
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e37-46
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1
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