Natural history and galsulfase treatment in mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrome)--10-year follow-up of patients who previously participated in an MPS VI Survey Study. (Q52902721)
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scientific article published on 24 April 2014
Language | Label | Description | Also known as |
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English | Natural history and galsulfase treatment in mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrome)--10-year follow-up of patients who previously participated in an MPS VI Survey Study. |
scientific article published on 24 April 2014 |
Statements
Natural history and galsulfase treatment in mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrome)--10-year follow-up of patients who previously participated in an MPS VI Survey Study. (English)
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Roberto Giugliani
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Christina Lampe
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Nathalie Guffon
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David Ketteridge
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Elisa Leão-Teles
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James E Wraith
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Simon A Jones
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Cheri Piscia-Nichols
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Ping Lin
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Adrian Quartel
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Paul Harmatz
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24 April 2014
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164A
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1953-1964
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8
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Identifiers
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