Pompe disease: Design, methodology, and early findings from the Pompe Registry (Q57639968)

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author name string

Barry J. Byrne

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Priya S. Kishnani

2

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Wolfgang Müller-Felber

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Suyash Prasad

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Ans van der Ploeg

Molecular Genetics and Metabolism

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publication date

May 2011

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published in

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volume

103

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page(s)

1-11

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issue

1

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cites work

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