Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (Q65348064)

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clinical trial
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English
Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy
clinical trial

    Statements

    Long-Term Observational Study of Translarna Safety and Effectiveness in Usual Care (English)
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    April 2015
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    April 2022
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    200
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