Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (Q65348064)
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clinical trial
Language | Label | Description | Also known as |
---|---|---|---|
English | Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy |
clinical trial |
Statements
Long-Term Observational Study of Translarna Safety and Effectiveness in Usual Care (English)
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April 2015
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April 2022
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200
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