Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells (Q24634829)

Stefan J Marciniak

13

0 references

Ignacio Varela

Ignacio Varela

4

0 references

James P Di Santo

James P Di Santo

17

0 references

Ludovic Vallier

Ludovic Vallier

20

0 references

Helene Strick-Marchand

Helene Strick-Marchand

3

0 references

David E Paschon

6

David E Paschon

0 references

Pei-Qi Liu

5

Pei-Qi Liu

0 references

author name string

Kosuke Yusa

1

0 references

S Tamir Rashid

2

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Adriana Ordóñez

8

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Nicholas R F Hannan

9

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Foad J Rouhani

10

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Sylvie Darche

11

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Graeme Alexander

12

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Noemi Fusaki

14

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Mamoru Hasegawa

15

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Michael C Holmes

16

0 references

David A Lomas

18

0 references

Allan Bradley

A conditional knockout resource for the genome-wide study of mouse gene function

19

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language of work or name

English

0 references

publication date

20 October 2011

0 references

published in

Nature

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volume

478

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issue

7369

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page(s)

391-4

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cites work

1 reference

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7 April 2017

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7 April 2017

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Zinc finger-DNA recognition: crystal structure of a Zif268-DNA complex at 2.1 A

7 April 2017

1 reference

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Induction of pluripotent stem cells from adult human fibroblasts by defined factors

7 April 2017

1 reference

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Induced pluripotent stem cell lines derived from human somatic cells

7 April 2017

1 reference

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Genome editing with engineered zinc finger nucleases

7 April 2017

1 reference

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Highly efficient endogenous human gene correction using designed zinc-finger nucleases

7 April 2017

1 reference

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Engineering polydactyl zinc-finger transcription factors

7 April 2017

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Efficient induction of transgene-free human pluripotent stem cells using a vector based on Sendai virus, an RNA virus that does not integrate into the host genome

7 April 2017

1 reference

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Treatment of sickle cell anemia mouse model with iPS cells generated from autologous skin

7 April 2017

1 reference

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A ROCK inhibitor permits survival of dissociated human embryonic stem cells

7 April 2017

1 reference

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A highly efficient recombineering-based method for generating conditional knockout mutations

7 April 2017

1 reference

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Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases

7 April 2017

1 reference

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A hyperactive piggyBac transposase for mammalian applications

7 April 2017

1 reference

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Induced pluripotency: history, mechanisms, and applications

27 September 2017

1 reference

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Modeling inherited metabolic disorders of the liver using human induced pluripotent stem cells.

27 September 2017

1 reference

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A rapid and general assay for monitoring endogenous gene modification

27 September 2017

1 reference

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Genome modification in human embryonic stem cells

27 September 2017

1 reference

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Gene targeting of a disease-related gene in human induced pluripotent stem and embryonic stem cells

27 September 2017

1 reference

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Conformational pathology of the serpins: themes, variations, and therapeutic strategies

27 September 2017

1 reference

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Human embryonic stem cells reveal recurrent genomic instability at 20q11.21.

27 September 2017

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Recurrent chromosomal abnormalities in human embryonic stem cells

27 September 2017

1 reference

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Autophagic disposal of the aggregation-prone protein that causes liver inflammation and carcinogenesis in alpha-1-antitrypsin deficiency

27 September 2017

1 reference

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Chromosomal transposition of PiggyBac in mouse embryonic stem cells

27 September 2017

1 reference

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Generation of an inducible and optimized piggyBac transposon system.

27 September 2017

1 reference

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Tools for targeted manipulation of the mouse genome

27 September 2017

1 reference

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Precise excision of TTAA-specific lepidopteran transposons piggyBac (IFP2) and tagalong (TFP3) from the baculovirus genome in cell lines from two species of Lepidoptera

27 September 2017

1 reference

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Generation of functional hepatocytes from human embryonic stem cells under chemically defined conditions that recapitulate liver development

27 September 2017

1 reference

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Generation of transgene-free induced pluripotent mouse stem cells by the piggyBac transposon

30 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3198846

The challenge of immunogenicity in the quest for induced pluripotency.

30 May 2018

1 reference

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Short DNA sequences inserted for gene targeting can accidentally interfere with off-target gene expression.

21 January 2018

1 reference

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Preserving the genetic integrity of human embryonic stem cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNATURE10424

Generation of induced pluripotent stem cells from human terminally differentiated circulating T cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNATURE10424

Adaptation to culture of human embryonic stem cells and oncogenesis in vivo

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21993621

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

An efficient and reversible transposable system for gene delivery and lineage-specific differentiation in human embryonic stem cells

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21993621

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/NATURE10424

1 reference

Dimensions Publication ID

1303894

1038728338

0 references

1303894

1 reference

1 reference

1 reference