Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study (Q28141072)
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English | Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study |
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Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study (English)
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Richard S Finkel
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Claudia A Chiriboga
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Jiri Vajsar
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John W Day
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Jacqueline Montes
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Darryl C De Vivo
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Mason Yamashita
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Frank Rigo
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Gene Hung
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Eugene Schneider
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Daniel A Norris
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Shuting Xia
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C Frank Bennett
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Kathie M Bishop
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6 December 2016
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388
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3017-3026
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10063
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Identifiers
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